Biomedical Engineering Reference
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References
1. Gaudet D, Methot J, Dery S et al (2013)
Effi cacy and long-term safety of alipogene
tiparvovec (AAV1-LPLS447X) gene therapy
for lipoprotein lipase defi ciency: an open-label
trial. Gene Ther 20:361-369
2. Kaplitt MG, Feigin A, Tang C et al (2007)
Safety and tolerability of gene therapy with an
adeno-associated virus (AAV) borne GAD
gene for Parkinson's disease: an open label,
phase I trial. Lancet 369:2097-2105
3. Hermens WT, Ter BO, Dijkhuizen PA et al
(1999) Purifi cation of recombinant adeno-
associated virus by iodixanol gradient ultracen-
trifugation allows rapid and reproducible
preparation of vector stocks for gene transfer
in the nervous system. Hum Gene Ther 10:
1885-1891
4. Kaplitt MG, Leone P, Samulski RJ et al (1994)
Long-term gene expression and phenotypic
correction using adeno-associated virus vec-
tors in the mammalian brain. Nat Genet
8:148-154
5. McCown TJ, Xiao X, Li J et al (1996)
Differential and persistent expression patterns
of CNS gene transfer by an adeno-associated
virus (AAV) vector. Brain Res 713:99-107
6. Peel AL, Zolotukhin S, Schrimsher GW et al
(1997) Effi cient transduction of green fl uores-
cent protein in spinal cord neurons using
adeno-associated virus vectors containing cell
type-specifi c promoters. Gene Ther 4:16-24
7. Hoke A (2006) Mechanisms of Disease: what
factors limit the success of peripheral nerve
regeneration in humans? Nat Clin Pract
Neurol 2:448-454
8. Macgillavry HD, Stam FJ, Sassen MM et al
(2009) NFIL3 and cAMP response
element-binding protein form a transcriptional
feedforward loop that controls neuronal
regeneration-associated
12. Li S, Liu Q, Wang Y et al (2013) Differential
gene expression profi ling and biological pro-
cess analysis in proximal nerve segments after
sciatic nerve transection. PLoS One 8:e57000
13. Verhaagen J, Van Kesteren RE, Bossers KA
et al (2012) Molecular target discovery for
neural repair in the functional genomics era.
Handb Clin Neurol 109:595-616
14. Beutler AS, Reinhardt M (2009) AAV for pain:
steps towards clinical translation. Gene Ther
16:461-469
15. Mingozzi F, High KA (2011) Therapeutic
in
vivo
gene transfer for genetic disease using
AAV: progress and challenges. Nat Rev Genet
12:341-355
16. Ginn SL, Alexander IE, Edelstein ML et al
(2013) Gene therapy clinical trials worldwide
to 2012 - an update. J Gene Med 15:65-77
17. Mason MR, Ehlert EM, Eggers R et al (2010)
Comparison of AAV serotypes for gene deliv-
ery to dorsal root ganglion neurons. Mol Ther
18:715-724
18. Naldini L, Blomer U, Gallay P et al (1996)
In
vivo
gene delivery and stable transduction of
nondividing cells by a lentiviral vector. Science
272:263-267
19. Yu H, Fischer G, Jia G et al (2011) Lentiviral
gene transfer into the dorsal root ganglion of
adult rats. Mol Pain 7:63
20. Storek B, Harder NM, Banck MS et al (2006)
Intrathecal long-term gene expression by self-
complementary adeno-associated virus type 1
suitable for chronic pain studies in rats. Mol
Pain 2:4
21. Storek B, Reinhardt M, Wang C et al (2008)
Sensory neuron targeting by self-
complementary AAV8 via lumbar puncture for
chronic pain. Proc Natl Acad Sci U S A
105:1055-1060
22. Towne C, Pertin M, Beggah AT et al (2009)
Recombinant adeno-associated virus serotype
6 (rAAV2/6)-mediated gene transfer to noci-
ceptive neurons through different routes of
delivery. Mol Pain 5:52
23. Xu Q, Chou B, Fitzsimmons B et al (2012)
In
vivo
gene knockdown in rat dorsal root ganglia
mediated by self-complementary adeno-
associated virus serotype 5 following intrathe-
cal delivery. PLoS One 7:e32581
24. Malkmus SA, Yaksh TL (2004) Intrathecal
catheterization and drug delivery in the rat.
Methods Mol Med 99:109-121
25. Yaksh TL, Rudy TA (1976) Chronic catheter-
ization of the spinal subarachnoid space.
Physiol Behav 17:1031-1036
gene
expression.
J Neurosci 29:15542-15550
9. Stam FJ, Macgillavry HD, Armstrong NJ et al
(2007) Identifi cation of candidate transcrip-
tional modulators involved in successful regen-
eration after nerve injury. Eur J Neurosci 25:
3629-3637
10. Geeven G, Macgillavry HD, Eggers R et al
(2011) LLM3D: a log-linear modeling-based
method to predict functional gene regulatory
interactions from genome-wide expression
data. Nucleic Acids Res 39:5313-5327
11. Arthur-Farraj PJ, Latouche M, Wilton DK
et al (2012) c-Jun reprograms Schwann cells of
injured nerves to generate a repair cell essential
for regeneration. Neuron 75:633-647
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