The Potential of Gene and Cell- Based Strategies for the Treatment of Osteogenesis Imperfecta - Osteogenesis Imperfecta - page 493

[77] Caulield T, McGuire A. Athletes' use of unproven stem cell
therapies: adding to inappropriate media hype? Mol Ther 2012;
20(9):1656-8.
[78] Cyranoski D. Stem cells in Texas: cowboy culture. Nature
2013;494(7436):166-8.
[79] Le Blanc K, Gotherstrom C, Ringden O, Hassan M, McMahon R,
Horwitz E, et al. Fetal mesenchymal stem-cell engraftment in bone
after in utero transplantation in a patient with severe osteogenesis
imperfecta. Transplantation 2005;79(11):1607-14.
[80] Panaroni C, Gioia R, Lupi A, Besio R, Goldstein SA, Kreider J, et al.
In utero transplantation of adult bone marrow decreases perinatal
lethality and rescues the bone phenotype in the knockin murine
model for classical, dominant osteogenesis imperfecta. Blood
2009;114(2):459-68.
[81] Vanleene M, Saldanha Z, Cloyd KL, Jell G, Bou-Gharios G,
Bassett JH, et al. Transplantation of human fetal blood stem cells
in the osteogenesis imperfecta mouse leads to improvement in
multiscale tissue properties. Blood 2011;117(3):1053-60.
[82] Olson SD, Pollock K, Kambal A, Cary W, Mitchell GM, Tempkin J,
et al. Genetically engineered mesenchymal stem cells as a pro-
posed therapeutic for Huntington's disease. Mol Neurobiol
2012;45(1):87-98.
[83] Voswinkel J, Francois S, Simon JM, Benderitter M, Gorin NC,
Mohty M, et al. Use of mesenchymal stem cells (MSC) in chronic
inflammatory fistulizing and fibrotic diseases: a comprehensive
review. Clin Rev Allergy Immunol. 2013 Jan 8. [Epub ahead of
print] PMID: 23296948.

[87] Takahashi KTK, Ohnuki M, Narita M, Ichisaka T, Tomoda K,
Yamanaka S. Induction of pluripotent stem cells from adult
human ibroblasts by deined factors. Cell 2007;131(5):861-72.
[88] Yu JVM, Smuga-Otto K, Antosiewicz-Bourget J, Frane JL, Tian S,
Nie J, et al. Induced pluripotent stem cell lines derived from
human somatic cells. Science 2007;318(5858):1917-20.
[89] Robinton DA, Daley GQ. The promise of induced pluripotent
stem cells in research and therapy. Nature 2012;481(7381):295-305.
[90] Yamanaka S. Induced pluripotent stem cells: past, present and
future. Cell Stem Cell 2012;10:678-84.
[91] Soldner F, Laganiere J, Cheng AW, Hockemeyer D, Gao Q,
Alagappan R, et al. Generation of isogenic pluripotent stem cells
differing exclusively at two early onset Parkinson point muta-
tions. Cell 2011;146(2):318-31.
[92] Hockemeyer D, Wang H, Kiani S, Lai CS, Gao Q, Cassady JP,
et al. Genetic engineering of human pluripotent cells using
TALE nucleases. Nat Biotechnol 2012;29(8):731-4.
[93] Ohtsuka M, Miura H, Gurumurthy CB, Kimura M, Inoko H,
Yoshimura S, et al. Fluorescent transgenic mice suitable for
multi-color aggregation chimera studies. Cell Tissue Res
2012;350(2):251-60.
[94] Ushiku C, Adams D, Jiang X, Wang L, Rowe D. Long bone frac-
ture repair in mice harboring GFP reporters for cells within the
osteoblastic lineage. J Orthop Res 2010;28(10):1338-47.
[95] Murao H, Yamamoto K, Matsuda S, Akiyama H. Periosteal cells
are a major source of soft callus in bone fracture. J Bone Miner
Metab. 2013 Mar 12. [Epub ahead of print] PMID: 23475152.

[84] Barcala Tabarrozzi AE, Castro CN, Dewey RA, Sogayar MC,

Labriola L, Perone MJ. Cell-based interventions to halt auto-
immunity in type 1 diabetes mellitus. Clin Exp Immunol 2013;
171(2):135-46.

[96] Shultz LD, Ishikawa F, Greiner DL. Humanized mice in transla-

tional biomedical research. Nat Rev Immunol 2007;7(2):118-30.

[97] Garcia S, Freitas AA. Humanized mice: current states and per-

spectives. Immunol Lett 2012;146(1-2):1-7.

[85] Li F, Wang X, Niyibizi C. Bone marrow stromal cells contribute

to bone formation following infusion into femoral cavities of a
mouse model of osteogenesis imperfecta. Bone 2010;47(3):546-55.

[98] Hockemeyer D, Soldner F, Beard C, Gao Q, Mitalipova M,

DeKelver RC, et al. Eficient targeting of expressed and silent
genes in human ESCs and iPSCs using zinc-inger nucleases.
Nat Biotechnol 2009;27(9):851-7. [86] Wilmut I, Sullivan G, Taylor J. A decade of progress since the

birth of Dolly. Reprod Fertil Dev 2009;21(1):95-100.